Global Orphan Drugs Market Insights, Forecast to 2034
Published on: 2024-01-04 | No of Pages : 400 | Industry : Pharma & Healthcare
Publisher : MRA | Format : PDF
Global Orphan Drugs Market Insights, Forecast to 2034
Orphan drugs are medicines that are used to treat diseases that cannot be produced profitably without the assistance of the government because there are so few patients. Conditions that are treated are known as rare diseases.
Market Analysis and InsightsGlobal Orphan Drugs Market
Global Orphan Drugs market is expected to reach to US$ million in 2023, with a positive growth of %, compared with US$ million in 2024 which suffered dual impact of COVID-19 and Russia-Ukraine War in the year. Backed with the increasing demand from downstream industries, Orphan Drugs industry is evaluated to reach US$ million in 2034. The CAGR will be % during 2023 to 2034.
Globally, Orphan Drugs key companies include Amber Specialty Pharmacy, Alexion Pharmaceuticals (Astra AB), Johnson & Johnson, Novartis, Celgene (Bristol-Myers Squibb), AbbVie, GSK, Roche and Sanofi, etc. Amber Specialty Pharmacy, Alexion Pharmaceuticals (Astra AB), Johnson & Johnson are top 3 players and held % share in total in 2024.
When considering the consumption regions, % revenue of Orphan Drugs were sold to North America, Europe and Asia Pacific in 2024. Asia Pacific is estimated to experience fast growth, with the CAGR of % during 2023 to 2034 and the share will be % in 2034. Moreover, China, plays a key role in the whole Orphan Drugs market and estimated to attract more attentions from industry insiders and investors.
Orphan Drugs can be divided into Biopharmaceutical and Other, etc. Biopharmaceutical is the mainstream product in the market, accounting for % revenue share globally in 2024 and the proportion will be % in 2034.
Orphan Drugs is widely used in various fields, such as Child and Aldult, etc. Child provides greatest supports to the Orphan Drugs industry development. In 2024, global % revenue of Orphan Drugs went into Child filed and the proportion will reach to % in 2034.
Report Covers
This report presents an overview of global Orphan Drugs market from 2018 to 2034, aiming to help readers to get a comprehensive understanding of global Orphan Drugs market with multiple angles. Items like regional revenue from 2018 to 2034 and companies’ revenue and gross margin from 2018 to 2023 are analyzed. In addition, revenue of product type and application in each region from 2018 to 2034 are also highlighted.
Companies, Type, Application and Regions Listed in the Report

Amber Specialty Pharmacy
Alexion Pharmaceuticals (Astra AB)
Johnson & Johnson
Novartis
Celgene (Bristol-Myers Squibb)
AbbVie
GSK
Roche
Sanofi
Pfizer
Vertex
Merck & Co.
Segment by Type
Biopharmaceutical
Other
Child
Aldult
By Region
North America
United States
Canada
Europe
Germany
France
UK
Italy
Russia
Nordic Countries
Rest of Europe
China
Asia (excluding China)
Japan
South Korea
China Taiwan
Southeast Asia
India
Latin America, Middle East & Africa
Brazil
Mexico
Turkey
Israel
GCC Countries
Chapter 1Product definition, type and application introduction
Chapter 2Regional revenue analysis from 2018 to 2034
Chapter 3Detailed analysis of Product Name companies’ competitive landscape, revenue, market share and industry ranking, latest development plan, merger, and acquisition information, etc.
Chapter 4Product revenue analysis by type from 2018 to 2034 globally
Chapter 5Product revenue analysis by application from 2018 to 2034 globally
Chapter 6Product revenue analysis by type and application from 2018 to 2034 in US & Canada. Product revenue analysis of each country in US & Canada from 2018 to 2034
Chapter 7Product revenue analysis by type and application from 2018 to 2034 in Europe. Product revenue analysis of each country in Europe from 2018 to 2034
Chapter 8Product revenue analysis by type and application from 2018 to 2034 in China. Product revenue analysis of China from 2018 to 2034
Chapter 9Product revenue analysis by type and application from 2018 to 2034 in Asia (excluding China). Product revenue analysis of each country in Asia (excluding China) from 2018 to 2034
Chapter 10Product revenue analysis by type and application from 2018 to 2034 in Middle East, Africa and Latin America. Product revenue analysis of each country in Middle East, Africa and Latin America from 2018 to 2034.
Chapter 11Companies’ outline, covering company’s basic information, major business, Orphan Drugs introduction, etc. Orphan Drugs Revenue and Gross Margin of each company from 2018 to 2023
Chapter 12Mr Accuracy reports’s Conclusions of Orphan Drugs
Chapter 13Methodology and Data Sources adopted by Mr Accuracy reports
Market Analysis and InsightsGlobal Orphan Drugs Market
Global Orphan Drugs market is expected to reach to US$ million in 2023, with a positive growth of %, compared with US$ million in 2024 which suffered dual impact of COVID-19 and Russia-Ukraine War in the year. Backed with the increasing demand from downstream industries, Orphan Drugs industry is evaluated to reach US$ million in 2034. The CAGR will be % during 2023 to 2034.
Globally, Orphan Drugs key companies include Amber Specialty Pharmacy, Alexion Pharmaceuticals (Astra AB), Johnson & Johnson, Novartis, Celgene (Bristol-Myers Squibb), AbbVie, GSK, Roche and Sanofi, etc. Amber Specialty Pharmacy, Alexion Pharmaceuticals (Astra AB), Johnson & Johnson are top 3 players and held % share in total in 2024.
When considering the consumption regions, % revenue of Orphan Drugs were sold to North America, Europe and Asia Pacific in 2024. Asia Pacific is estimated to experience fast growth, with the CAGR of % during 2023 to 2034 and the share will be % in 2034. Moreover, China, plays a key role in the whole Orphan Drugs market and estimated to attract more attentions from industry insiders and investors.
Orphan Drugs can be divided into Biopharmaceutical and Other, etc. Biopharmaceutical is the mainstream product in the market, accounting for % revenue share globally in 2024 and the proportion will be % in 2034.
Orphan Drugs is widely used in various fields, such as Child and Aldult, etc. Child provides greatest supports to the Orphan Drugs industry development. In 2024, global % revenue of Orphan Drugs went into Child filed and the proportion will reach to % in 2034.
Report Covers
This report presents an overview of global Orphan Drugs market from 2018 to 2034, aiming to help readers to get a comprehensive understanding of global Orphan Drugs market with multiple angles. Items like regional revenue from 2018 to 2034 and companies’ revenue and gross margin from 2018 to 2023 are analyzed. In addition, revenue of product type and application in each region from 2018 to 2034 are also highlighted.
Companies, Type, Application and Regions Listed in the Report

By Company
Amber Specialty Pharmacy
Alexion Pharmaceuticals (Astra AB)
Johnson & Johnson
Novartis
Celgene (Bristol-Myers Squibb)
AbbVie
GSK
Roche
Sanofi
Pfizer
Vertex
Merck & Co.
Segment by Type
Biopharmaceutical
Other
Segment by Application
Child
Aldult
By Region
North America
United States
Canada
Europe
Germany
France
UK
Italy
Russia
Nordic Countries
Rest of Europe
China
Asia (excluding China)
Japan
South Korea
China Taiwan
Southeast Asia
India
Latin America, Middle East & Africa
Brazil
Mexico
Turkey
Israel
GCC Countries
Chapter Outline
Chapter 1Product definition, type and application introduction
Chapter 2Regional revenue analysis from 2018 to 2034
Chapter 3Detailed analysis of Product Name companies’ competitive landscape, revenue, market share and industry ranking, latest development plan, merger, and acquisition information, etc.
Chapter 4Product revenue analysis by type from 2018 to 2034 globally
Chapter 5Product revenue analysis by application from 2018 to 2034 globally
Chapter 6Product revenue analysis by type and application from 2018 to 2034 in US & Canada. Product revenue analysis of each country in US & Canada from 2018 to 2034
Chapter 7Product revenue analysis by type and application from 2018 to 2034 in Europe. Product revenue analysis of each country in Europe from 2018 to 2034
Chapter 8Product revenue analysis by type and application from 2018 to 2034 in China. Product revenue analysis of China from 2018 to 2034
Chapter 9Product revenue analysis by type and application from 2018 to 2034 in Asia (excluding China). Product revenue analysis of each country in Asia (excluding China) from 2018 to 2034
Chapter 10Product revenue analysis by type and application from 2018 to 2034 in Middle East, Africa and Latin America. Product revenue analysis of each country in Middle East, Africa and Latin America from 2018 to 2034.
Chapter 11Companies’ outline, covering company’s basic information, major business, Orphan Drugs introduction, etc. Orphan Drugs Revenue and Gross Margin of each company from 2018 to 2023
Chapter 12Mr Accuracy reports’s Conclusions of Orphan Drugs
Chapter 13Methodology and Data Sources adopted by Mr Accuracy reports
